Chemotherapy Drugs of Choice

 

Adrenocortical
Anal
Biliary tract
Bladder
   superficial
   systemic
Brain
   anaplastic astrocytoma/gliob
   anaplastic oligodendroglioma
   medulloblastoma
   germ cell tumors
   primary CNS lymphoma
Breast
   risk reduction
   adjuvant
   metastatic
Carcinoid
Cervix
   locally advanced
   metastatic
Choriocarcinoma
Colorectal
   adjuvant
   metastatic
Endometrial
Esophageal
Ewing's sarcoma
Gastric
Head and neck
Hepatoblastoma
Islet cell
Kaposi's Sarcoma
Leukemias
   ALL induction
   ALL CNS prophylaxis
   ALL maintenance
   AML Induction
   AML CNS prophylaxis
   APL
   CLL
   CML-CP
   CML-AP
   CML blast phase (lymph)
   CML blast phase (myeloid)
   Hairy cell
Liver
Lung
   non-small cell
   small cell
Melanoma
   adjuvant
   metastatic
Multiple myeloma
Neuroblastoma
Osteosarcoma
Ovarian
   germ cell
   epithelial
Pancreatic
   adjuvant
   localized unresectable
   metastatic
Pheochromocytoma
Prostate
Renal
Retinoblastoma
Rhabdomyosarcoma
Sarcoma, soft tissue
Testicular
Thyroid (anaplastic)
Wilms' tumor

 

Adrenocortical
Mitotane
Cisplatin +/- etoposide

Alternatives:
Doxorubicin

 

Anal
Fluorouracil + mitomycin

Alternatives:
Cisplatin

 

Biliary tract
Fluorouracil +/- leucovorin

Alternatives:
Fluorouracil + doxorubicin + mitomycin (FAM)
Cisplatin
Gemcitabine

 

Bladder (superficial)
BCG instillation

Alternatives:
Instilled mitomycin, doxorubicin, thiotepa, or valrubicin

 

Bladder (systemic)
MTX + vinblastine + doxorubicin + cisplatin (MVAC)

Alternatives:
Cisplatin + MTX + vinblastine (CMV)
Paclitaxel + carboplatin
Gemcitabine + cisplatin
Ifosfamide + mesna
Gallium nitrate

 

Anaplastic astrocytoma/glioblastoma
Procarbazine + lomustine + vincristine
Carmustine wafers

Alternatives:
Temozolomide
Carmustine
Cisplatin or carboplatin

 

Anaplastic oligodendroglioma
Procarbazine + lomustine + vincristine

Alternatives:
Carmustine
Cisplatin

 

Medulloblastoma/embryonal
Lomustine + cisplatin + vincristine
Vincristine + cisplatin + cyclophosphamide + etoposide

Alternatives:
Lomustine + vincristine + prednisone

 

Germ cell tumors
Cisplatin + etoposide
Carboplatin + etoposide

Alternatives:
Vinblastine
Bleomycin
Cyclophosphamide

 

Primary CNS lymphoma
High-dose IV MTX + IT MTX
High-dose IV cytarabine

Alternatives:
BBB disruption w/ IV cyclophosphamide, intra-arterial MTX + leucovorin, and oral procarbazine and dexamethasone

 

Breast (risk reduction)
Tamoxifen

 

Breast (adjuvant)
Doxorubicin + cyclophosphamide +/- fluorouracil (AC or CAF), followed by paclitaxel
Cyclophosphamide + MTX + fluorouracil (CMF)
Tamoxifen for ER+ and hormone-responsive

Alternatives:
Cyclophosphamide + epirubicin + fluorouracil (CEF)

 

Breast (metastatic)
Doxorubicin + cyclophosphamide +/- fluorouracil (AC or CAF)
Cyclophosphamide + MTX + fluorouracil (CMF)
Tamoxifen or toremifene for ER+ and/or hormone responsive
Paclitaxel + trastuzumab for HER2 overexpression

Alternatives:
Paclitaxel
Docetaxel
Capecitabine
Vinorelbine
Mitoxantrone
Epirubicin
Fluorouracil CI
Anastrazole, letrozole, or examustine
Megestrol acetate
Fluoxymesterone

 

Carcinoid
Fluorouracil + streptozocin
Doxorubicin

Alternatives:
Dacarbazine
Interferon alfa
Octreotide for carcinoid syndrome

 

Cervix (locally advanced)
Cisplatin +/- fluorouracil

Alternatives:
Carboplatin
Fluorouracil
Epirubicin
Paclitaxel
Doxorubicin
Vinblastine
MTX
Mitomycin
Irinotecan

 

Cervix (metastatic)
Cisplatin
Ifosfamide with mesna
Bleomycin + ifosfamide/mesna + cisplatin (BIP)

Alternatives:
Carboplatin
Fluorouracil
Epirubicin
Paclitaxel
Doxorubicin
Vinblastine
MTX
Mitomycin
Irinotecan

 

Choriocarcinoma
MTX +/- leucovorin
Dactinomycin

Alternatives:
Etoposide + MTX + dactinomycin + cyclophosphamide + vincristine (EMA-CO)
MTX + dactinomycin + cyclophosphamide (MAC)
Cisplatin +/- etoposide

 

Colorectal (adjuvant)
Fluorouracil + leucovorin

 

Colorectal (metastatic)
Fluorouracil + leucovorin + irinotecan

Alternatives:
Capecitabine
Oxaliplatin
Tegafur/uracil + leucovorin

 

Endometrial
Doxorubicin + cisplatin +/- cyclophosphamide
Megestrol or other progestin

Alternatives:
Epirubicin
Tamoxifen
Carboplatin
Paclitaxel

 

Esophageal
Cisplatin + fluorouracil

Alternatives:
Paclitaxel
Doxorubicin
MTX
Vinorelbine
Bleomycin
Irinotecan

 

Ewing's sarcoma
Vincristine + doxorubicin + cyclophosphamide, alternating with ifosfamide/mesna + etoposide

Alternatives:
Dactinomycin

 

Gastric
Fluorouracil +/- leucovorin

Alternatives:
Fluorouracil + doxorubicin + MTX (FAMTX) or mitomycin (FAM)
Infusional fluorouracil + cisplatin
Etoposide
Paclitaxel
Docetaxel
Irinotecan + cisplatin

 

Head and neck
Cisplatin + fluorouracil or paclitaxel

Alternatives:
Docetaxel
MTX
Bleomycin
Carboplatin
Ifosfamide

 

Hepatoblastoma
Vincristine + cisplatin + fluorouracil
Cisplatin + doxorubicin

Alternatives:
Etoposide
Carboplatin
Ifosfamide/mesna

 

Islet cell
Streptozocin + doxorubicin

Alternatives:
Streptozocin + fluorouracil
Chlorozotocin
Dacarbazine
Interferon alpha

 

Kaposi's Sarcoma
Liposomal doxorubicin or daunorubicin
Doxorubicin + bleomycin + vincristine (ABV)

Alternatives:
Vinblastine
Etoposide
Interferon alpha
Paclitaxel
Vinorelbine
Alitretinoin gel

 

Leukemias

ALL induction
Vincristine + prednisone + asparaginase + daunorubicin or doxorubicin +/- cyclophosphamide

Alternatives:
Same, +/- high-dose MTX +/- cytarabine
Tenopiside or etoposide
High-dose cytarabine + mitoxantrone
Ifosfamide/mesna


ALL CNS prophylaxis
IT MTX +/- IT cytarabine +/- IT hydrocortisone +/- high-dose systemic MTX/leucovorin


ALL maintenance
Mercaptopurine + MTX

Alternatives:
Same, plus monthly vincristine and prednisone


AML induction
Cytarabine + either daunorubicin or idarubicin +/- etoposide

Alternatives:
High-dose cytarabine + daunorubicin or idarubicin
Vincristine, cyclophosphamide, MTX, mitoxantrone, fludarabine, carboplatin, topotecan, gemtuzumab


AML CNS prophylaxis

IT cytarabine or MTX +/- IT hydrocortisone


AML post-induction
High-dose cytarabine +/- other drugs

Alternatives:
Vincristine, cyclophosphamide, MTX, mitoxantrone, fludarabine, carboplatin, topotecan, gemtuzumab


APL
Tretinoin +/- further induction therapy

Alternatives:
Arsenic trioxide


CLL
Fludarabine +/- cyclophosphamide
Chlorambucil or cyclophosphamide +/- prednisone

Alternatives:
Cyclophosphamide + vincristine + prednisone +/- doxorubicin
Cladribine
Pentostatin


CML chronic phase
Interferon alfa +/- cytarabine

Alternatives:
Hydroxyurea
Busulfan
Homoharringtonine


CML accelerated phase
Cytarabine + daunorubicin or idarubicin

Alternatives:
Hydroxyurea
Busulfan
Interferon alfa


CML blast phase (lymphoid)
Vincristine + prednisone + asparaginase + doxorubicin or daunorubicin +/- cyclophosphamide + IT MTX +/- maintenance with mercaptopurine + MTX

Alternatives:
Azacitidine
Vincristine +/- plicamycin
STI-571


CML blast phase (myeloid)
Cytarabine + daunorubicin or idarubicin


Hairy cell
Cladribine
Pentastatin

Alternatives:
Interferon alfa

 

Liver
Hepatic intra-arterial floxuridine, cisplatin, doxorubicin, or mitomycin

Alternatives:
Doxorubicin
Fluorouracil

 

Lung (non-small cell)
Paclitaxel + cisplatin or carboplatin
Cisplatin + vinorelbine
Gemcitabine + cisplatin

Alternatives:
Mitomycin + vinblastine + cisplatin (MVP)
Mitomycin + ifosfamide/mesna + cisplatin (MIC)
Docetaxel
Irinotecan
Cisplatin + etoposide
Vinorelbine

 

Lung (small cell)
Cisplatin or carboplatin + etoposide (PE)

Alternatives:
Topotecan
Cyclophosphamide + doxorubicin + vincristine (CAV)

 

Melanoma (adjuvant)
Interferon alpha

 

Melanoma (metastatic)
Dacarbazine

Alternatives:
Dacarbazine + cisplatin + vinblastine +/- interferon alpha + interleukin-2

 

Multiple myeloma
Melphalan or cyclophosphamide + prednisone
Vincristine + doxorubicin + dexamethasone (VAD)

Alternatives:
Vincristine + carmustine + melphalan + cyclophosphamide + prednisone (VBMCP)
Etoposide + dexamethasone + cytarabine +cisplatin (EDAP)
High-dose dexamethasone
Interferon alpha
Thalidomide

 

Neuroblastoma
Doxorubicin + cyclophosphamide + cisplatin + etoposide or teniposide

Alternatives:
Carboplatin
Vincristine
Topotecan

 

Osteosarcoma
High-dose MTX + doxorubicin + cisplatin

Alternatives:
Doxorubicin + cisplatin + MTX + ifosfamide/mesna
Etoposide + ifosfamide/mesna
Ifosfamide/mesna + cisplatin + etoposide (ICE)
Dactinomycin
Vincristine

 

Ovarian (germ cell)
Bleomycin + etoposide + cisplatin (BEP)

Alternatives:
Vincristine + dactinomycin + cisplatin
Etoposide + cisplatin or carboplatin

 

Ovarian (epithelial)
Cisplatin or carboplatin + paclitaxel

Alternatives:
Topotecan
Cyclophosphamide
Ifosfamide/mesna
Tamoxifen
Melphalan
Altretamine
Oral etoposide
Docetaxel
Liposomal doxorubicin
Gemcitabine
Interferon gamma

 

Pancreatic (adjuvant)
Fluorouracil

Alternatives:
Doxorubicin
Mitomycin

 

Pancreatic (localized unresectable)
Fluorouracil

Alternatives:
Doxorubicin
Mitomycin

 

Pancreatic (metastatic)
Gemcitabine

 

Pheochromocytoma
Cyclophosphamide + vincristine + dacarbazine (CVD)

Alternatives:
Streptozocin

 

Prostate
Leuprolide or goserelin +/- flutamide or bicalutamide or nilutamide

Alternatives:
Mitoxantrone + prednisone
Estramustine + docetaxel or vinblastine or paclitaxel
Doxorubicin + ketoconazole
Ketoconazole + prednisone
Megestrol acetate

 

Renal
Interleukin-2

Alternatives:
Interferon alpha

 

Retinoblastoma
Doxorubicin + cyclophosphamide +/- vincristine +/- cisplatin +/- etoposide
IT MTX +/- cytarabine +/- hydrocortisone

Alternatives:
Carboplatin
Ifosfamide/mesna

 

Rhabdomyosarcoma
Vincristine + dactinomycin + either cyclophosphamide (VAC ) or ifosfamide/mesna

Alternatives:
Doxorubicin
Melphalan
Cisplatin
Etoposide

 

Sarcoma, soft tissue
Ifosfamide/mesna + doxorubicin +/- dacarbazine


Alternatives:
Doxorubicin + cisplatin + mitomycin
Vincristine
Cyclophosphamide
Epirubicin

 

Testicular
Cisplatin + etoposide +/- bleomycin (PEB)

Alternatives:
Ifosfamide/mesna + cisplatin + etoposide or vinblastine
Gemcitabine
Paclitaxel

 

Thyroid (anaplastic)
Doxorubicin
Cisplatin

 

Wilms' tumor
Dactinomycin + vincristine +/- doxorubicin +/- cyclophosphamide

Alternatives:
Ifosfamide/mesna
Etoposide
Carboplatin or cisplatin


Adapted from: The Medical Letter; Vol 42(1087-1088), September 18, 2000
© 2000-2006 Pharmacy OneSource, Inc.